A newborn boy with unusual bleeding symptoms was diagnosed with a rare form of von Willebrand disease (VWD) linked to two inherited variants in…
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The lack of a key enzyme in thrombotic thrombocytopenic purpura (TTP) may threaten fetal survival during pregnancy, according to a study involving rats. Researchers…
Spleen tyrosine kinase (SYK) inhibitors, including Tavalisse (fostamatinib disodium hexahydrate), may be effective treatments for adults with chronic primary ITP,…
Cases of immune-mediated thrombotic thrombocytopenic purpura (iTTP) rose in Germany from 2011 to 2021, with patients also experiencing more severe complications despite advances in…
Six people with treatment-resistant immune thrombocytopenia (ITP) and underlying systemic lupus erythematosus (SLE) all achieved clinical responses to CAR T-cell immunotherapy, according to a…
Star Therapeutics‘ experimental therapy VGA039, developed to prevent bleeding in von Willebrand disease (VWD), has been granted both rare pediatric disease and breakthrough…
A man’s severe case of treatment-resistant immune thrombotic thrombocytopenic purpura (iTTP) — which resulted in severe anemia despite more than a week spent in…
People diagnosed with immune thrombotic thrombocytopenic purpura (TTP) in the U.S. report significant unmet healthcare needs, particularly related to mental health support and relapse…
A woman with an extremely rare combination of three autoimmune diseases — immune thrombocytopenia (ITP), autoimmune hemolytic anemia (AIHA), and antiphospholipid syndrome — has been…
Taking both laboratory parameters and genetic testing into account can improve diagnostic accuracy in people with von Willebrand disease (VWD), according to a study…
