OK given for testing higher dose of ITP treatment CID-103 in study
Casi Pharmaceuticals has been given the all-clear to start dosing a fifth group of patients in a clinical trial testing its treatment candidate CID-103…
News
FDA expands Vonvendi approval to cover more VWD patients
The U.S. Food and Drug Administration (FDA) has expanded its approval of Vonvendi (recombinant von Willebrand factor), a treatment for von Willebrand disease (VWD).
Combination therapy works to treat acquired TTP patients in India
Using both corticosteroids and plasma exchange therapy — each a standard treatment for acquired thrombotic thrombocytopenic purpura (TTP) — together was found to significantly…
Tailored blood thinning helps man, 65, with ITP, recurrent strokes
A man in his 60s with immune thrombocytopenia (ITP) experienced repeated strokes even while taking anticoagulant medications — commonly known as blood thinners —…
Research finds bleeding severity varies widely in type 2 VWD
The severity of bleeding in type 2 von Willebrand disease (VWD) can vary widely between subtypes and even among patients who carry the same…
TTP symptoms vary, but prevention helps control them: Study
The congenital form of thrombotic thrombocytopenic purpura (TTP) can look very different in one person than in another, but preventive treatment can help reduce…
ITP Awareness Month focuses attention on rare bleeding disorder
Patients, caregivers, medical professionals, and other advocates are coming together in September for Immune Thrombocytopenia Awareness Month to raise awareness and support for a…
Impacts on quality of life of children with VWD vary based on age
Children with von Willebrand disease (VWD) have reduced health-related quality of life, although the specific areas that seem to be most affected depend on…
1st BTK inhibitor rilzabrutinib, now Wayrilz, approved in US for ITP
Note: This story was updated Sept. 2, 2025, to clarify the definition of a durable platelet response used in LUNA 3. The U.S. Food and…
An early diagnosis helps woman with TTP deliver healthy baby
A woman in Spain delivered a full-term, healthy baby after she was identified early as having congenital thrombotic thrombocytopenic purpura (TTP) and treated successfully…
