Wayrilz recommended for approval in Europe to treat ITP
An arm of the European Medicines Agency (EMA) is recommending that Wayrilz (rilzabrutinib) be approved to treat adults with immune thrombocytopenia (ITP) who…
Marisa Wexler MS, —
Articles by Marisa Wexler
Preclinical study points to new way to treat VWD type 1
Researchers created an experimental treatment for von Willebrand disease (VWD) type 1 that aims to stabilize the protein whose defect causes the disease, increasing…
Switching to Adzynma slashes hospital stays in congenital TTP
Switching from treatment with fresh frozen plasma (FFP) to Adzynma (ADAMTS13, recombinant-krhn) can help people with congenital thrombotic thrombocytopenic purpura (TTP) avoid hospital stays,…
Star Therapeutics raises $125M to advance bleeding treatment
Star Therapeutics has raised $125 million to support the development of VGA039, a treatment for von Willebrand disease (VWD) and other bleeding disorders…
Low-dose drug combo may be effective treatment for ITP
Combining low-dose eltrombopag with reduced-dose prednisone may be an effective approach for controlling immune thrombocytopenia (ITP) while minimizing the risk of medication side effects,…
ITP treatments may raise clotting risk after spleen removal: Study
People with immune thrombocytopenia (ITP) who have had their spleens surgically removed may face an increased risk of clotting problems from ITP treatments…
Drug combo doesn’t stem VWD postpartum bleeding, trial finds
Adding Cyklokapron (tranexamic acid) to Vonvendi (recombinant von Willebrand factor) does not appear to reduce blood loss following childbirth for women with von Willebrand…
OK given for testing higher dose of ITP treatment CID-103 in study
Casi Pharmaceuticals has been given the all-clear to start dosing a fifth group of patients in a clinical trial testing its treatment candidate CID-103…
FDA expands Vonvendi approval to cover more VWD patients
The U.S. Food and Drug Administration (FDA) has expanded its approval of Vonvendi (recombinant von Willebrand factor), a treatment for von Willebrand disease (VWD).
Combination therapy works to treat acquired TTP patients in India
Using both corticosteroids and plasma exchange therapy — each a standard treatment for acquired thrombotic thrombocytopenic purpura (TTP) — together was found to significantly…
